CRISPR activation rescues abnormalities in SCN2A haploinsufficiency-associated autism spectrum disorder
Authors
Serena Tamura,
Andrew NelsonPerry Spratt,
Henry Kyoung,
Xujia Zhou,
Zizheng Li,
Zhao Jin,
Stephanie Holden,
Atehsa Sahagun,
Caroline Keeshen,
Congyi Lu,
Elizabeth Hamada,
Roy Ben-Shalom,
Jen Pan,
Jeanne Paz,
Stephan Sanders,
Navneet Matharu,
Nadav Ahituv +16 authors
,
Kevin Bender Tip Tip