mRNA therapy restores ureagenesis and corrects glutathione metabolism in argininosuccinic aciduria
Authors
Sonam Gurung,
Oskar TimmermandDany Perocheau,
Ana Gil-Martínez,
Magdalena Minnion,
Loukia Touramanidou,
Sherry Fang,
Martina Messina,
Youssef Khalil,
A. Barber,
Richard Edwards,
Patrick Finn,
Alex Cavedon,
Summar Siddiqui,
Lisa Rice,
Paolo Martini,
Philippa Mills,
Simon Waddington,
Paul Gissen,
Simon Eaton,
Mina Ryten,
Martin Feelisch,
Andrea Frassetto,
Timothy Witney,
Julien Baruteau +23 authors
,
Abigail Barber Tip Tip