Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

Authors

Naoki Iwamoto

Published

June 11, 2024

Abstract

Huntington's disease (HD) is an autosomal dominant disease caused by the expansion of cytosine-adenine-guanine (CAG) repeats in one copy of the

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Support the authors with ResearchCoin

Journal

Molecular Therapy — Nucleic Acids

Topics

DOI

10.1016/j.omtn.2024.102246

License

CC-BY-NC-ND

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

Authors

Naoki Iwamoto

Published

June 11, 2024

Abstract

Huntington's disease (HD) is an autosomal dominant disease caused by the expansion of cytosine-adenine-guanine (CAG) repeats in one copy of the

Supporters

Support the authors with ResearchCoin

Journal

Molecular Therapy — Nucleic Acids

Topics

DOI

10.1016/j.omtn.2024.102246

License

CC-BY-NC-ND

Paper

Paper

Paper

Paper

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

Abstract

Supporters

Journal

Topics

DOI

License

Preclinical evaluation of stereopure antisense oligonucleotides for allele-selective lowering of mutant HTT

Abstract

Supporters

Journal

Topics

DOI

License

Supporters

Journal

Topics

DOI

License