PTC124 targets genetic disorders caused by nonsense mutations
Authors
Ellen Welch,
Elisabeth BartonJ. Zhuo,
Yuki Tomizawa,
Westley Friesen,
Panayiota Trifillis,
Sergey Paushkin,
Meenal Patel,
Christopher Trotta,
Seongwoo Hwang,
Richard Wilde,
Gary Karp,
James Takasugi,
Guangming Chen,
Stephen Jones,
Hongyu Ren,
Young‐Choon Moon,
Donald Corson,
Anthony Turpoff,
Jeffrey Campbell,
M. Conn,
Atiyya Khan,
Neil Almstead,
Jean Hedrick,
Anna Mollin,
Nicole Risher,
Marla Weetall,
Shirley Yeh,
Art Branstrom,
Joseph Colacino,
John Babiak,
William Ju,
Samit Hirawat,
Valerie Northcutt,
Langdon Miller,
Phyllis Spatrick,
Feng He,
Masataka Kawana,
Huisheng Feng,
Allan Jacobson,
Stuart Peltz,
H. Sweeney +40 authors
,
Jin Zhuo Tip Tip