SMN2 splice modulators enhance U1–pre-mRNA association and rescue SMA mice
Authors
James Palacino,
Susanne SwalleyCheng Song,
Atwood Cheung,
Lei Shu,
Xiaolu Zhang,
Mailin Hoosear,
Youngah Shin,
Donovan Chin,
Caroline Keller,
Martin Beibel,
Nicole Renaud,
Thomas Smith,
Michael Salcius,
Xiaoying Shi,
Marc Hild,
Rebecca Servais,
Monish Jain,
Lin Deng,
Caroline Bullock,
Michael McLellan,
Sven Schuierer,
Leo Murphy,
Marcel Blommers,
Cecile Blaustein,
Frada Berenshteyn,
Arnaud Lacoste,
Jason Thomas,
Guglielmo Roma,
Gregory Michaud,
Brian Tseng,
Jeffery Porter,
Vic Myer,
John Tallarico,
Lawrence Hamann,
Daniel Curtis,
Mark Fishman,
William Dietrich,
Natalie Dales +37 authors
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Rajeev Sivasankaran Tip Tip