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Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neur... | ResearchHub
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Intrathecal 2-hydroxypropyl-β-cyclodextrin decreases neurological disease progression in Niemann-Pick disease, type C1: a non-randomised, open-label, phase 1–2 trial
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Authors
Daniel Ory
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Daniel Ory
•
Elizabeth Ottinger
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•
Forbes Porter
Published
August 11, 2017
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Journal
The Lancet
Topics
Chemistry
Biochemistry
Medicine
Physiology
Internal Medicine
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DOI
10.1016/s0140-6736(17)31465-4
