Transplantation of Genetically Corrected Human iPSC-Derived Progenitors in Mice with Limb-Girdle Muscular Dystrophy
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Authors
Francesco Tedesco
Francesco Tedesco•Emanuela Longa•Giulio Cossu
Published
June 27, 2012
Abstract
Genetically corrected mesoangioblasts from human iPSCs derived from limb-girdle muscular dystrophy patients produce muscle fibers expressing the therapeutic gene in a mouse model of the disease.
