Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy
Authors
Richard Finkel,
Eugenio MercuriBasil Darras,
Anne Connolly,
Nancy Kuntz,
Janbernd Kirschner,
Claudia Chiriboga,
Kayoko Saito,
Laurent Servais,
Eduardo Tizzano,
Haluk Topaloğlu,
M. Tulinius,
Jacqueline Montes,
Allan Glanzman,
Kathie Bishop,
Zhensbao Zhong,
Sarah Gheuens,
C. Bennett,
Eugene Schneider,
Wildon Farwell +18 authors
,
Darryl Vivo Tip Tip