Somatic gene editing ameliorates skeletal and cardiac muscle failure in pig and human models of Duchenne muscular dystrophy
Authors
Alessandra Moretti,
Lina FonteyneFlorian Giesert,
Petra Hoppmann,
Anna Meier,
Tarik Bozoglu,
Andrea Baehr,
Christine Schneider,
Daniel Sinnecker,
Katharina Klett,
Thomas Fröhlich,
Farah Rahman,
Tobias Haufe,
Shicheng Sun,
Victoria Jurisch,
Barbara Keßler,
Rabea Hinkel,
Ralf Dirschinger,
Eimo Martens,
Clemens Jilek,
Alexander Graf,
Stefan Krebs,
Gianluca Santamaria,
Mayuko Kurome,
Valeri Zakhartchenko,
Birgit Campbell,
K. Voelse,
Anja Wolf,
Tilman Ziegler,
Stefan Reichert,
S. Lee,
Florian Flenkenthaler,
Tatjana Dorn,
Irmela Jeremias,
Helmut Blum,
Andreas Dendorfer,
Angelika Schnieke,
Sabine Krause,
Maggie Walter,
Nikolai Klymiuk,
Karl‐Ludwig Laugwitz,
Eckhard Wolf,
Wolfgang Wurst +41 authors
,
Christian Kupatt Tip Tip