Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials
Authors
Paula Rı́o,
Josune ZubicaraySusana Navarro,
Eva Gálvez,
Rebeca Sánchez‐Domínguez,
Eileen Nicoletti,
Elena Sebastián,
Michael Rothe,
Roser Pujol,
Massimo Bogliolo,
Philipp John-Neek,
Antonella Bastone,
Axel Schambach,
Wei Wang,
Manfred Schmidt,
Lise Larcher,
José Segovia,
Rosa Yáñez,
Omaira Alberquilla,
Begoña Díez,
María Fernández-García,
Laura García‐García,
Manuel Ramı́rez,
Anne Galy,
François Lefrère,
Marina Cavazzana,
Thierry Leblanc,
Nagore Andoín,
Ricardo Almaraz,
Albert Català,
Jordi Barquinero,
Sandra Rodríguez,
Gayatri Rao,
Jordi Surrallés,
Jean Soulier,
Cristina Heredia,
Jonathan Schwartz,
Julián Sevilla,
Juan Bueren +37 authors
,
Albert Catalá Tip Tip